About the Disease
Phenylketonuria (PKU) is a type of amino acid metabolism disorder that is inherited, preventing the body from processing part of a protein called phenylalanine (Phe). If the Phe level gets too high, it can damage the brain and cause severe intellectual disability. All babies born in U.S. hospitals must now have a screening test for PKU, making it easier to diagnose and treat the problem early. The most severe form of this disorder is known as classic PKU, and without treatment, children develop permanent intellectual disability. Seizures, delayed development, behavioral problems, and psychiatric disorders are also common.
About our Patient Care
Our dedicated Care Team will work with the physician's office and insurance on a patient's behalf so that our patients have more time to focus on their treatment and quality of life. We are here to listen, provide
counseling on treatment, including side-effect management, and assist with sourcing third-party financial assistance.
As part of treatment, we provide:
Dedicated Care Team
We provide prescribers and patients with a dedicated care team for each of our disease state programs. This includes a primary pharmacy contact, clinical education, side-effects management, scheduled refill calls, and a direct phone, fax and email address.
In-Home Patient- and Family-Centric Care
We administer a nationwide nursing network, allowing patients to pursue in-home treatment or receive training on self-administrated drugs. Our nurses are ideally positioned to establish a partnership with patients and their families in order to provide clinical education and coaching that strengthen the patient's capacity to achieve therapy goals.
Shipping and Coordination of Care
We provide free overnight delivery of medications and necessary medical supplies and manage the coordination of care between prescribers, sites of care, nurses and patients to ensure dispenses and drug delivery align with the date and location of service.
We successfully identify and assist enrolling patients into any and all manufacturer co-pay and foundation support programs in order to minimize a potential financial burden to patients given the high-cost of specialty medications.
24/7/365 Access to a Pharmacist
We provide prescribers and patients access to a pharmacist 24/7/365 to ensure patients are always cared for.
Kuvan (sapropterin dihydrochloride)
Brand Name | Kuvan
Manufacturer | Biomarin
Route of Administration | Oral
Approved Indication | Reduce blood Phe levels in people with a certain type of Phenylketonuria (PKU)
Self-Administration | Yes
Product Website |www.kuvan.com